Study to Evaluate the Efficacy and Safety of Intravitreal OTX-TKI (Axitinib Implant) in Subjects With Neovascular Age- Related Macular Degeneration

Recruitment Status
ACTIVE, NOT RECRUITING
(See Contacts and Locations)Verified May 2025 by Ocular Therapeutix, Inc.
Sponsor
Ocular Therapeutix, Inc.
Information Provided by (Responsible Party)
Ocular Therapeutix, Inc.
Clinicaltrials.gov Identifier
NCT06495918
Other Study ID Numbers:
OTX-TKI-2023-AMD-303
First Submitted
July 2, 2024
First Posted
July 10, 2024
Last Update Posted
June 16, 2025
Last Verified
May 2025

ClinicalTrials.gov processed this data on June 2025Link to the current ClinicalTrials.gov record .

History of Changes

Study Details

Study Description

Condition or DiseaseIntervention/Treatment
Neovascular Age-related Macular Degeneration
Drug: OTX-TKIDrug: AfliberceptDrug: Aflibercept

Study Design

Study TypeInterventional
Actual Enrollment825 participants
Design AllocationRandomized
Interventional ModelParallel Assignment
MaskingQuadruple
Primary PurposeTreatment
Official TitleA Phase 3, Multicenter, Double-Masked, Randomized, Parallel Group Study to Evaluate the Efficacy and Safety of Intravitreal OTX-TKI (Axitinib Implant) in Subjects With Neovascular Age- Related Macular Degeneration
Study Start DateNovember 26, 2024
Actual Primary Completion Date8mos 5d from now
Actual Study Completion Date8mos 5d from now

Groups and Cohorts

Group/CohortIntervention/Treatment
OTX-TKI Re-dose
Drug: OTX-TKI
Intravitreal Injection of OTX-TKI
Aflibercept 2mg on label
Drug: Aflibercept
Intravitreal Injection of 2mg of aflibercept
Aflibercept 8mg high dose
Drug: Aflibercept
Intravitreal Injection of 2mg of aflibercept

Outcome Measures

Primary Outcome Measures
  1. Best Corrected Visual Acuity (BCVA)
    Mean change in Best Corrected Visual Acuity (BCVA) from baseline at Week 48

Eligibility Criteria

Ages Eligible for Study(Adult, Older Adult)
Sexes Eligible for StudyAll
Accepts Healthy VolunteersNo
Inclusion Criteria
Treatment naïve juxtafoveal and/or SFNV secondary to Neovascular Age- Related Macular Degeneration (nAMD) with leakage involving the fovea in the study eye prior to Screening, or have a diagnosis of Neovascular Age- Related Macular Degeneration (nAMD) in study eye within 3 months prior to screening and received up to 2 monthly injections of 2 mg aflibercept with last injection approximately 4 weeks prior to Screening
Have provided written consent
Exclusion Criteria
Monocular subject or Best Corrected Visual Acuity (BCVA) score of \<20 ETDRS letters or 20/400 in fellow eye at Screening
Have evidence of a scar, fibrosis, or atrophy of \>50% of the total lesion in the study eye.

Contacts and Locations

Sponsors and CollaboratorsOcular Therapeutix, Inc.
Locations
Associated Retina Consultant | Gilbert Arizona, United States, 85297Associated Retina Consultants, Ltd. | Phoenix Arizona, United States, 85020Retinal Research Institute, LLC | Phoenix Arizona, United States, 85053Retina Macula Institute of Arizona | Scottsdale Arizona, United States, 85255California Retina Consultants | Bakersfield California, United States, 93309The Retina Partners | Encino California, United States, 91436Retina Consultants of Orange County | Fullerton California, United States, 92835Atlantis Eyecare | Huntington Beach California, United States, 92647Salehi Retina Institute, Inc., dba Retina Associates of Southern California | Huntington Beach California, United States, 92647Kaiser Permanente Division of Research | Oakland California, United States, 94611California Retina Consultants | Oxnard California, United States, 93036Stanford Health Care - Byers Eye Institute | Palo Alto California, United States, 94303Stanford University School of Medicine, Byers Eye Institute | Palo Alto California, United States, 94303California Eye Specialists Medical Group, INC | Pasadena California, United States, 91107Retinal Consultants Medical Group | Sacramento California, United States, 95841Orange County Retina Medical Group | Santa Ana California, United States, 92705California Retina Consultants | Santa Barbara California, United States, 93103Macula Retina Vitreous Research Institute | Torrance California, United States, 90503Bay Area Retina Associates | Walnut Creek California, United States, 94598Retina Consultants of Southern Colorado | Colorado Springs Colorado, United States, 80909RSC Research, LLC | Denver Colorado, United States, 80210Colorado Retina Associates | Lakewood Colorado, United States, 80228Retina Consultants, P.C | Manchester Connecticut, United States, 06042Retina Group of New England | Waterford Connecticut, United States, 06385Advanced Research LLC. | Deerfield Beach Florida, United States, 33064Rand Eye Institute | Deerfield Beach Florida, United States, 33064Retina Group of Florida | Fort Lauderdale Florida, United States, 33308Florida Retina Consultants | Lakeland Florida, United States, 33805South Florida Retina Institute | Miami Florida, United States, 33145Florida Retina Institude | Orlando Florida, United States, 32806Retina Specialty Institute | Pensacola Florida, United States, 32503MedEye Associates | South Miami Florida, United States, 33143Retina Vitreous Associates of Florida- Saint Petersburg | St. Petersburg Florida, United States, 33711Retina Vitreous Associates of Florida | Tampa Florida, United States, 33617Southeast Retina Center | Augusta Georgia, United States, 30909University Retina and Macula Associates, PC | Oak Forest Illinois, United States, 60452Illinois Retina Associates | Oak Park Illinois, United States, 60304Springfield Clinic Opthalmology Department | Springfield Illinois, United States, 62703Associate Vitreoretinal and Uveitis Consultants | Carmel Indiana, United States, 46032Retina Partners Midwest, P.C. | Carmel Indiana, United States, 46290Retina Partners Midwest | Indianapolis Indiana, United States, 46290Wolfe Clinic PC dba Wolfe Eye Clinic | West Des Moines Iowa, United States, 50026The Retina Group of Washington - Chevy Chase | Chevy Chase Maryland, United States, 20815Cumberland Valley Retina Consultants | Hagerstown Maryland, United States, 21740Mid Atlantic Retina Specialists | Hagerstown Maryland, United States, 21740Retina Specialists - Towson Office | Towson Maryland, United States, 21204Associated Retinal Consultants, P.C. | Royal Oak Michigan, United States, 48073Retina Consultants of Minnesota | Minneapolis Minnesota, United States, 55435Mississippi Retina Associates | Madison Mississippi, United States, 39110The Retina Institute | St Louis Missouri, United States, 63128Sierra Eye Associates | Reno Nevada, United States, 89502Envision Ocular, LLC | Bloomfield New Jersey, United States, 07003Vision Research Center Eye Associates of New Mexico | Albuquerque New Mexico, United States, 87109Retina Vitreous Surgeons of CNY, PC | Liverpool New York, United States, 13088Asheville Eye Associates (AEA) - Asheville | Asheville North Carolina, United States, 28803Cincinnati Eye Institute | Cincinnati Ohio, United States, 45242EyeHealth Northwest | Portland Oregon, United States, 97225Erie Retina Research | Erie Pennsylvania, United States, 16507Palmetto Retina Center, LLC | Aiken South Carolina, United States, 29802Charleston Neuroscience Instititute, LLC | Beaufort South Carolina, United States, 29902Palmetto Retina Center, LLC | Florence South Carolina, United States, 29501Palmetto Retina Center, LLC | West Columbia South Carolina, United States, 29169Black Hills Regional Eye Institute, LLP | Rapid City South Dakota, United States, 57701Charles Retina Institute | Germantown Tennessee, United States, 38138Southeastern Retina Associates PC | Johnson City Tennessee, United States, 37604Tennessee Retina, PC | Nashville Tennessee, United States, 37203Retina Research Institute of Texas | Abilene Texas, United States, 79606Texas Retina Associates | Arlington Texas, United States, 76012Austin Research Center for Retina | Austin Texas, United States, 78705Austin Retina Associates | Austin Texas, United States, 78705Retina Consultants of Texas | Beaumont Texas, United States, 77707Retina Consultants of Texas | Bellaire Texas, United States, 77401Star Vision Research | Burleson Texas, United States, 76028Texas Retina Associates | Dallas Texas, United States, 75231Texas Retina Center | Houston Texas, United States, 77030Retina Consultants of Texas | Katy Texas, United States, 77494Retina Consultants of Texas | San Antonio Texas, United States, 78240Retina Center of Texas | Southlake Texas, United States, 76092Retina Consultants of Texas | The Woodlands Texas, United States, 77384Retina Associates of Utah | Salt Lake City Utah, United States, 84107Rocky Mountain Retina Consultants | Salt Lake City Utah, United States, 84107Retina Group of Washington | Fairfax Virginia, United States, 22031Vistar Eye Center | Roanoke Virginia, United States, 24019Eye Clinic of Wisconsin, SC | Wausau Wisconsin, United States, 54403Organización Médica de Investigación (OMI) | Buenos Aires , Argentina, 1015Centro Privado de Ojos | Buenos Aires , Argentina, C1033AAWCharles Research Center (Centro Oftalmologico Dr. Charles S.A) | Buenos Aires , Argentina, C1121ABBBuenos Aires Macula | Caba , Argentina, C1061AAEInstituto Oftalmologico de Buenos Aires SA - OFTALMOS | Caba , Argentina, C1120AANFundacion Zambrano - Cirugia Ocular | Caba , Argentina, SFundacion Jorge Zambrano para la investigacion, Diagnostico y Tratamiento de las enfermedades oculares | Ciudad Autonoma de Buenos Aire , Argentina, C1023AAQOftar Mendoza Srl Centro Privado de Oftalmologia | Mendoza , Argentina, M5500GGKCentro Vision S.A. | Mendoza , Argentina, M5500Laser Vision Group | Rosario , Argentina, S2000Albury Eye Clinic | Albury New South Wales, Australia, 2640Marsden Eye Specialists (MES) - Parramatta | Parramatta New South Wales, Australia, 2150Emanuelli Research and Development Center, LLC | Arecibo , Puerto Rico, 612
Investigators
Principal Investigator: Dilsher Dhoot, MD, California Retina Consultants (CRC) - Santa Barbara